Stephen Simpson, CFA
Long only, growth at reasonable price, value, research analyst

PTC Therapeutics Looks Like A High-Risk Play On Rare Diseases

With money and momentum flowing out of the biotech sector, there are going to be a lot of beaten-down diamonds in the rough amidst the wreckage. I'm not entirely convinced PTC Therapeutics (NASDAQ:PTCT) is a diamond, or at least not yet. While the company's lead compound ataluren has a lot of promise, there some serious questions and concerns about the drug. Bulls are right about the high-end potential here, but prior trial failures shouldn't be ignored.

Is Ataluren A Big Deal Or Nonsense?

PTC Therapeutics believes that its lead drug ataluren could address numerous monogenic diseases caused by nonsense mutations. These conditions are caused by point mutations in the DNA sequence that cause premature stop codons, resulting in...

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