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Sunday, Sep 22
Alexion's asfotase alfa meets primary endpoint in hypophosphatasia study
- Researchers have presented data from a Phase 2 study of Alexion Pharmaceuticals' (ALXN) targeted enzyme replacement therapy asfotase alfa in children and infants with hypophosphatasia.
- The study met its primary endpoint of improving skeletal mineralization from baseline.
- Improvement was observed as soon as 12 weeks and continued at 48 weeks, with 93% of those treated surviving the first four years of treatment.
- The drug has a Breakthrough Therapy designation. (PR)