PTC Therapeutics expects EMA committee opinion on AADC deficiency gene therapy in May

Apr. 14, 2022 9:27 AM ETPTC Therapeutics, Inc. (PTCT)By: Anuron Mitra, SA News Editor
  • Biopharmaceutical company PTC Therapeutics (NASDAQ:PTCT) on Thursday said it has completed procedural meetings for its gene therapy treatment for (AADC) deficiency with the European Union drug regulator's Committee for Advanced Therapies (CAT).
  • The CAT will provide its opinion for adoption of the therapy to the European Union drug regulator's Committee for Medicinal Products for Human Use in May.
  • PTCT's gene therapy treats aromatic L-amino acid decarboxylase (AADC) deficiency, a rare and fatal genetic disorder that typically causes severe disability from the first months and years of life.

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